A compact Cas12f nuclease shows high editing efficiency in human cells, with structural insights enabling an engineered variant potentially suited for future AAV‑compatible delivery.

The CRISPR-Cas gene-editing system has long been the focus of research as a promising tool in genome editing. However, the ...

The draft guidance supports the agency’s new pathway designed to speed up the development of custom gene therapies.

Scientists have taken an important step toward a gene therapy that could one day turn off the extra genetic material that ...

The document outlines the non-clinical sequencing and bioinformatics data sponsors need to submit as part of INDs and BLAs for gene-editing therapies.

The document outlines the non-clinical sequencing and bioinformatics data sponsors need to submit as part of INDs and BLAs for gene-editing therapies.

Could the White House be overly optimistic about inflation? If so, you may want to own these stocks.

There are plenty of reasons, though, to be bullish on the stock, not the least of which is its improved cash position. The ...

Scientists are laying the groundwork for treating one of the most common genetic conditions in humans. Research out today ...

A research team has discovered an enhanced CRISPR gene-editing system that could enable targeted delivery inside the human ...